Tag Archives: First

FDA Approves Piqray (alpelisib) as First PI3K Inhibitor for Breast Cancer

FDA Approves Piqray (alpelisib) as First PI3K Inhibitor for Breast Cancer Print this page May 24, 2019 — Today, the U.S. Food and Drug Administration approved Piqray (alpelisib) tablets, to be used in combination with the FDA-approved endocrine therapy fulvestrant, to treat postmenopausal women, and men, with hormone receptor (HR)-positive, human epidermal growth factor receptor 2… Read More »

First US attempt to cure a rare disease with genome editing fails miserably 

First US attempt to cure a rare disease with genome editing fails miserably Scientists at Sangamo attempted the first human trial of a gene-editing method to cure rare, debilitating enzyme deficiency diseases  After showing early promise, the DNA replacement failed to reduce levels of harmful unprocessed sugars  The gene replacement itself worked, but after nearly… Read More »